Day One
Vector Development

• Viral & non-viral vector safety & quality 

• Delivery and dosage challenges for gene therapies 

• Effective testing, characterisation & validation approaches 

Gene Therapy Manufacturing

• Scalable and cost-effective production processes 

• Balancing speed-to-market and product quality 

• Internal vs external manufacturing 

Pre-Clinical & Clinical Gene Therapy

• CAR-T, TCR & Engineered NK cell therapies 

• Applications of gene therapy in clinical research 

• Challenges from clinic to commercialization 

 
Day Two 
Gene Editing Technologies

• CRISPR, ZFNs, TALENS 

• Translating gene editing to the clinic 

• Standardisation & quality control for gene editing 

Gene Therapy Analytics & CMC

• Bioassays & analytical chemistry 

• Developing advanced analytical characterization methods 

• Tools to predict patient response to gene therapy 

Donna McLaren - Vice President at Orchard Therapeutics

Nripen Singh - Director, Technical Development at PassageBio

Simon Briggs - Head of Gene Therapy Technical Product at Biogen

Lisa Kirkwood - Senior Expert Science & Technology at Novartis

Anthony Newcombe - Chief Operating Officer at VectorY

Elise Huang - Group Leader at UCB