GTCbio, Boston, MA
2013-05-08 to 213-5-10
GTC is proud to announce its inaugural Orphan Drugs Research and Commercialization Conference at a crucial time in the rare disease space. With new therapies emerging in rare disease treatment and exciting partnerships being forged between big pharma and smaller niche companies, it is clear that the field of rare disease and orphan drug is growing. Rather than merely reciting the challenges of orphan drug development, it is time all stakeholders in the community come together to find innovative solutions in order to better serve rare disease patients. This meeting connects industry, academia, regulators, and patient groups to dialogue about strategies to improve orphan drug research, pricing, reimbursement, access, and other key topics. The Orphan Drugs Research and Commercialization Conference is one of four parallel tracks to the 2nd Novel Technologies in Drug Discovery Summit on May 8 - 10, 2013 in Boston, MA. Tentative Sessions Include:
Pre-Conference Workshop: Developing an Effective Pricing and Reimbursement Strategy Novel Therapeutics in Rare Diseases Designing Effective Clinical Trials Case Studies in the Preclinical and Clinical Space Partnering in Rare Diseases Commercialization of Orphan Drugs Panel Discussion: Regulatory in Orphan Drug Development
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Invited Speakers:
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Monica Coenraads Co-Founder & Executive Director Rett Syndrome Research Trust | | Tim Coté Professor of Practice, Regulatory Affairs Keck Graduate Institute | | Gerry Cox Vice President of Clinical Development, Rare Diseases Group Genzyme | | Christopher A. French Assistant Professor, Pathology Harvard Medical School and Brigham and Women's Hospital | | Pat Furlong Founding President & CEO Parent Project Muscular Dystrophy | | Cláudia Hirawat Senior Vice President, Corporate Development PTC Therapeutics | | Nicolas Koebel Global Commercial Lead, Rare Diseases GlaxoSmithKline | | Fulvio Mavilio Chief Scientific Officer Genethon | | Ramaiah Muthyala Associate Director, Center for Orphan Drug Development University of Minnesota | | May Orfali Senior Director, Rare Diseases Department Pfizer | | Stephanie Okey Vice President & General Manager, Rare Diseases, U.S Genetic Diseases Genzyme | | Douglas Paul Vice President & Partner Medical Marketing Economics, LLC | | Ian Phillips Norris Professor of Life Sciences & Director of the Center for Rare Disease Therapies Faculty Director Keck Graduate Institute | | Philip Vickers Senior Vice President, Research and Development |
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